ספריית מאמרים

How much dystrophin is needed for survival and function

מחקר מלווה בנושא הכשרת כלבי שירות לילדים ולאנשים עם מוגבלות פיזית

The 109 week treatment effects of viltolarsen

Children on performing the NSAA at home for children with Duchenne

Antisense and Gene Therapy Options for Duchenne Muscular Dystrophy Arising from Mutations in the N-Terminal Hotspot

An Open Label Exploratory Clinical Trial Evaluating Safety and Tolerability of Once-Weekly Prednisone in Becker and Limb-Girdle Muscular Dystrophy

BMI-z scores of boys with Duchenne muscular dystrophy already begin to increase before losing ambulation: a longitudinal exploration of BMI, corticosteroids and caloric intake

Repeated intravenous cardiosphere-derived cell therapy in late-stage Duchenne muscular dystrophy (HOPE-2): a multicentre, randomised, double-blind, placebo-controlled, phase 2 trial.

Growth pattern trajectories in boys with Duchenne muscular dystrophy

Interplay of disability, caregiver impact, and out-of-pocket expenditures in Duchenne muscular dystrophy: a cohort study

The Role of Taurine in Skeletal Muscle Functioning and Its Potential as a Supportive Treatment for Duchenne Muscular Dystrophy

Development of a novel startle response task in Duchenne muscular dystrophy

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